First for RNA therapy: man with rare motor-neuron disease improves after treatment
Nature, Published online: 18 September 2026; doi:10.1038/d41586-026-02945-zGene-targeting treatments could be used to treat other people with rare forms of amyotrophic lateral sclerosis (ALS).

<p>Nature, Published online: 18 September 2026; doi:10.1038/d41586-026-02945-zGene-targeting treatments could be used to treat other people with rare forms of amyotrophic lateral sclerosis (ALS).</p>